研究论文
Clinical application of base editing for treating β-thalassaemia
Yongrong Lai, Rongrong Liu, Lijie Wang, Xu-Kai Ma, Yaliang Li, Gaohui Yang, Lingling Shi, Yilin Guo 等 17 位
First Affiliated Hospital of GuangXi Medical University ShanghaiTech University Fudan University Children's Hospital of Fudan University
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逐年被引趋势
1790
1726
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17
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75.78
领域内被引倍数
同类平均 = 1
同类平均 = 1
前 0.1%
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同领域 · 同年份 · 同类型
同领域 · 同年份 · 同类型
63
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学术脉络
学科主题
生物医学Hemoglobinopathies and Related Disorders
Virus-based gene therapy research · CRISPR and Genetic Engineering
参考文献 63
Colony Forming Cell Assays for Human Hematopoietic Progenitor Cells
被引 33Bert Wognum, Ning Yuan, Becky Lai · Methods in molecular biology · 2012
BCL11A enhancer dissection by Cas9-mediated in situ saturating mutagenesis
被引 886Matthew C. Canver, Elenoe C. Smith, Falak Sher · Nature · 2015
Human Fetal Hemoglobin Expression Is Regulated by the Developmental Stage-Specific Repressor BCL11A
被引 918Vijay G. Sankaran, Tobias Menne, Jian Xu · Science · 2008
此处列出前 3 条
引用本文 17
Enhanced γ-globin reactivation and sickle cell correction through a repressor-to-activator motif switch in the HBG1/2 promoters
被引 4Anne Chalumeau, Panagiotis Antoniou, Maria Bou Dames · Molecular Therapy — Nucleic Acids · 2026
Clinical base editing for β-hemoglobinopathies across different genetic backgrounds
被引 2Rongrong Liu, Yongrong Lai, Lijie Wang · Cell stem cell · 2026
Efficient in vivo cytosine base editing using virus-like particles with uracil DNA glycosylase inhibition
被引 2Junjie Zhu, Lin Ding, Kexing Liu · Nature Biotechnology · 2026
按被引量排序，此处列出前 3 条